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48 Publications avec texte intégral

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DNM2 Gene therapy KLF15 CXCR4 Emerin Expanded repeats Exon skipping Chromatin Mdx Gut microbiota LTβR Dynamin 2 Cell Therapy Coculture Autophagy Gene Therapy Gel electrophoresis Dominant centronuclear myopathy Cell-penetrating peptide Folding-defective proteins Myotonic dystrophy Eteplirsen HDMD/Dmd-null mice DMD Adeno-associated viral vector BMD Glucose Lamina-associated domain MT RNA/DNA Editing Exondys 51 FSHD Exon Skipping Motor neuron Laminographie Fibrosis Insulin MSCs Fear response Actin Flavonoid Glucocorticoid-induced muscle atrophy Differentiation Muscle Neuromuscular junction Clinical trial candidate screening Immortalized dystrophic canine myoblast Human artificial chromosomes Lamin A/C nuclei Fibroblast CDNA synthesis Exon-skipping Alternative splicing Adhesion Mdx52 mice Dystrophin Migration Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Antisense morpholino CRISPR/Cas9 Developmental biology CLS Computer software Duchenne Muscular Dystrophy Myogenesis Antisense oligonucleotide Acetylcholine receptor subunit epsilon Skeletal muscle CXCL12 DsDNA break repair Human FoxO Human muscle stem/progenitor cells Allele-specific silencing therapy BAF CFTR correctors Lymphotoxin-β-receptor Allele-specific silencing Immortalisation CMS Duchenne muscular dystrophy RNA interference Drisapersen Canine X-linked muscular dystrophy in Japan CXMD J Gene network analysis Atrial cardiac defects ITSN1 3D co-culture LRP4 CTG⋅CAGn repeat Endocytosis Conjugation Bile acid Machine learning Becker muscular dystrophy Autophagosome Myotube Cell biology ICU-acquired weakness Centronuclear myopathy DM1 myoblasts